CRISPR-Edited Stem Cells and Sickle Cell Disease: A New Approach to Preventing Pain Crises
Editing Stem Cells to Change the Course of Disease Sickle cell disease is an inherited blood disorder that causes red blood cells to become rigid and misshapen. These abnormal cells can block blood flow, leading to painful episodes known as vaso-occlusive crises, along with anemia and damage to organs over time. A Phase 3 clinical…










